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    • A2 Biotherapeutics (1)
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    • Mucopolysaccharidosis II (MPS II) (Hunter Syndrome ) (3)
    • Mucopolysaccharidosis III (MPS III) (Sanfilippo Syndrome ) (1)
    • Multiple Myeloma (Kahler Disease) (1)
    • Multiple System Atrophy (MSA or Shy-Drager Syndrome or Multi-System Degeneration) (1)
    • Myasthenia Gravis (1)
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    • Narcolepsy (2)
    • Nasopharyngeal Cancer (2)
    • Natural Killer Cell Lymphomas (2)
    • Neisseria meningitidis Infections (1)
    • Netherton Syndrome (Trichorrhexis Invaginata, Bamboo Hair) (1)
    • Neurodegenerative Diseases (2)
    • Neurofibromatoses Type I (Von Recklinghausen’s Disease) (1)
    • Non Muscle Invasive Bladder Cancer (NMIBC) (Superficial Bladder Cancer) (1)
    • Non-Alcoholic Steatohepatitis (NASH) (3)
    • Non-Hodgkin Lymphoma (3)
    • Non-Small Cell Lung Cancer (12)
    • Non-Small Cell Lung Carcinoma (2)
    • Non-Small Cell Lung Carcinoma;Squamous Non-Small Cell Lung Carcinoma (1)
    • Norovirus Infections (1)
    • Obesity (4)
    • Ocular Melanoma (1)
    • Opium (Opioid) Addiction (1)
    • Ornithine-Transcarbamylase Deficiency (1)
    • Oropharyngeal Cancer (4)
    • Osteoarthritis (1)
    • Osteoarthritis Pain (1)
    • Otitis Externa (1)
    • Otitis Media (1)
    • Ovarian Cancer (2)
    • Pancreatic Cancer (2)
    • Pancreatic Ductal Adenocarcinoma (3)
    • Parkinson's Disease (5)
    • Paroxysmal Nocturnal Hemoglobinuria (1)
    • Pemphigus Vulgaris (1)
    • Penile Cancer (1)
    • Peripheral Neuropathy (Sensory Neuropathy) (1)
    • Peripheral T-Cell Lymphomas (PTCL) (1)
    • Phenylketonuria (PKU) (1)
    • Pituitary ACTH Hypersecretion (Cushing Disease) (1)
    • Plaque Psoriasis (Psoriasis Vulgaris) (2)
    • Polycythemia Vera (1)
    • Polyomavirus Infections (1)
    • Pompe Disease (1)
    • Porphyria (Erythropoietic Protoporphyri) (1)
    • Post Menopausal Osteoporosis (2)
    • Post-Essential Thrombocythemia Myelofibrosis (Post-ET MF) (3)
    • Post-Operative Pain (2)
    • Prader-Willi Syndrome (PWS) (1)
    • Presbyopia (1)
    • Primary Biliary Cholangitis (Primary Biliary Cirrhosis) (2)
    • Primary Hyperoxaluria Type I (1)
    • Primary Mediastinal B-Cell Lymphoma (3)
    • Primary Sjogren's Syndrome (1)
    • Prostate Cancer (1)
    • Pruritus (2)
    • Psoriatic Arthritis (1)
    • Psychosis (1)
    • Pulmonary Arterial Hypertension (1)
    • Pulmonary Hypertension (2)
    • Pulmonary Sarcoidosis (1)
    • Radiodermatitis (1)
    • Recurrent Glioblastoma Multiforme (GBM) (1)
    • Recurrent Head And Neck Cancer Squamous Cell Carcinoma (1)
    • Refractory Chronic Lymphocytic Leukemia (CLL) (1)
    • Refractory Multiple Myeloma (3)
    • Relapsed Acute Myeloid Leukemia (5)
    • Relapsed Chronic Lymphocytic Leukemia (CLL) (2)
    • Relapsed Multiple Myeloma (5)
    • Relapsed Multiple Myeloma;Refractory Multiple Myeloma (2)
    • Renal Cell Carcinoma (1)
    • Resistant Pseudomonas aeruginosa Infections (1)
    • Respiratory Syncytial Virus (RSV) Infections (3)
    • Rett Syndrome (1)
    • Rheumatoid Arthritis (5)
    • Rhinosinusitis (1)
    • Rubella (German Measles) (1)
    • Sarcomas (2)
    • Schizophrenia (1)
    • Secondary Acute Myeloid Leukemia (1)
    • Secondary Hyperoxaluria (1)
    • Sickle Cell Disease (4)
    • Skin Cancer (1)
    • Skin Rash (1)
    • Small-Cell Lung Cancer (4)
    • Solid Tumor (7)
    • Squamous Non-Small Cell Lung Cancer (3)
    • Squamous Non-Small Cell Lung Carcinoma (2)
    • Stammering (Stuttering) (1)
    • Streptococcal Pneumonia (2)
    • Supraventricular Tachycardia (1)
    • Surgical Wound Infections (1)
    • Synovial Sarcoma (1)
    • Systemic Lupus Erythematosus (2)
    • Systolic Heart Failure (3)
    • Thrombosis (1)
    • Transitional Cell Cancer (Urothelial Cell Cancer) (3)
    • Treatment Resistant Depression (4)
    • Triple-Negative Breast Cancer (TNBC) (2)
    • Type 1 Diabetes (Juvenile Diabetes) (4)
    • Type 2 Diabetes (3)
    • Ulcerative Colitis (4)
    • Upper Limb Muscle Spasticity (1)
    • Urinary Tract Infections (1)
    • Vaginal Cancer (1)
    • Varicella Zoster (HHV-3) Infections (1)
    • Ventilator Associated Pneumonia (VAP) (1)
    • Vulvar Cancer (1)
    • Waldenstrom Macroglobulinemia (Lymphoplasmacytic Lymphoma) (1)
    • Wet (Neovascular / Exudative) Macular Degeneration (3)
    • Xerostomia (1)

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    • A-2B530 (1)
    • ASP-2074 (1)
    • Zanzalintinib (1)