Ahead of Rare Disease Day, Abigail Beaney spoke with Robert Barrie and Frankie Fattorini on recent developments in the rare disease space.
Several new guidance documents issued by the FDA are poised to significantly impact the rare disease development landscape.
Généthon CEO Frédéric Revah says alternative patient access approaches are needed for ultra rare diseases.
The company anticipates the deal to positively impact operating income from fiscal 2028 onwards.
The agreement includes Ipsen’s investment in additional equipment at Quotient Sciences’ facility in Boothwyn, Pennsylvania, US.
The organised crime group were selling unlicensed weight loss-substances online, using social media to market products.
