FDA approves first gene therapy for Sanfilippo syndrome type A
The US Food and Drug Administration (FDA) has approved Ultragenyx’s gene therapy for Sanfilippo syndrome type A, marking the first…
News
Novo targets oral macrocycles with $1.4bn Orbis partnership
Ona Therapeutics to develop ADC with WuXi’s payload-linker platform
Roche agrees to $1bn deal with Dualitas for bispecific antibody research
Novo taps Anthropic’s Claude to ‘supercharge’ R&D efforts
Cellares and GenomeFrontier to assess automated GF-CART01 production
Viatris’ Wakix receives Japanese approval to treat OSAS and narcolepsy
Sling ropes in $123m for oral thyroid eye disease drug
