Oxford BioMedica has received US Food and Drug Administration (FDA) clearance for its Investigational New Drug (IND) application for the Phase I/IIa clinical development of UshStat, a gene-based therapy for the treatment of Usher syndrome 1B.
UshStat was developed using the company’s proprietary LentiVector platform technology to deliver a corrected version of the MYO7A gene to address the vision loss associated with the disease.
Go deeper with GlobalData
The open label, dose escalation Phase I/IIa study will enroll around 18 patients with Usher syndrome type 1B at Oregon Health and Science University’s Casey Eye Institute, Portland, Oregon, US.
The trial, which is likely to begin by the end of 2011, will assess three dose levels of UshStat for safety, tolerability and aspects of biological activity.
See Also:
How well do you really know your competitors?
Access the most comprehensive Company Profiles on the market, powered by GlobalData. Save hours of research. Gain competitive edge.
Thank you!
Your download email will arrive shortly
Not ready to buy yet? Download a free sample
We are confident about the unique quality of our Company Profiles. However, we want you to make the most beneficial decision for your business, so we offer a free sample that you can download by submitting the below form
By GlobalData
