Inside the efforts to rescue a rare disease gene therapy
Several patients are navigating ways to access innovative gene therapies with the help of enterprising research and nonprofit organisations.
29 July 2024
29 July 2024
Several patients are navigating ways to access innovative gene therapies with the help of enterprising research and nonprofit organisations.
The EMA recommended a label update that allows the drug to be used to reduce cardiovascular risk.
The ODAC highlighted that perioperative trials should separately evaluate the effectiveness of treatments pre- and post-operation.
The FDA approval is based on data gathered from two Phase III studies where over 30% of the patients gained 80% or more coverage of scalp hair.
Revenues saw a 9% increase, reaching $12.2bn from $11.2bn in Q2 2023.
The company has fired 25% of its staff and will look for partnerships to further its oncology candidates.
The current approval, which is based on data from non-human primates and healthy individuals, will be updated with real-world observations.
The new project is set to replace the high flux reactor, with operations commencing in the early 2030s.
Merging industry-leading business intelligence & award-winning journalism, this is an unrivalled opportunity for engagement with B2B professionals across a network of 40+ leading media websites.
Steer your business strategy with key data and insights from our latest market research reports and company profiles. Not ready to buy? Start small by downloading a sample report first.
Give your business an edge with our leading industry insights.