FDA layoffs and priority review programme’s lapse disrupt rare disease pipeline
The expiration of the FDA’s paediatric priority review voucher programme is creating uncertainty for rare disease drug developers.
24 April 2025
24 April 2025
The expiration of the FDA’s paediatric priority review voucher programme is creating uncertainty for rare disease drug developers.
The lawsuit filings are the latest turn in a long-running legal saga between GLP-1RAs makers and compounders.
AstraZeneca, Tempus and Pathos will develop an AI-driven foundational model to develop therapeutics in oncology.
Veraxa Biotech will gain access to $253m in cash from Voyager to advance its cancer drug pipeline.
Repertoire will obtain an upfront payment of $35m from Genentech, with the potential for up to $730m in additional milestones.
In a trial, patients showed neurological improvement when treated with the therapy versus a placebo.
The agreement facilitates EditCo to not only offer genomic knock-ins but also functional validation services.
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