19 September 2025
19 September 2025
Armed with fresh capital and new leadership, Genetix sharpens its gene therapy focus.
The study took place across multiple centres, as a double-blind, placebo-controlled trial, for 68 weeks.
Shape will obtain an initial payment and could potentially earn up to $1.2bn in combined fees and milestone payments.
By week 13, the 150mg daily dose led to a maximum mean weight loss of 14.8%.
FDA approvals in HAE were sparse before this year, with only one each in 2017, 2018, and 2020.
From a pharmaceutical strategy perspective, the findings elevate miR‑155 as a tissue‑level biomarker and potential target for early T1D intervention.
In preclinical models, rat insulinoma‑derived beta‑cell line INS‑1 (INS‑1) cells and mouse islets showed rapid, robust Viperin induction after cytokine exposure.
The move makes argenx the first announced tenant of FUJIFILM’s Phase II expansion at the location.
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