The Glycogen Storage Disorders (GSD) drugs in development market research report provides comprehensive information on the therapeutics under development for Glycogen Storage Disorders (GSD), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA), and molecule type. GlobalData’s report assesses key aspects of the companies and drugs in development for Glycogen Storage Disorders (GSD). Buy the report here.

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The report also covers the descriptive pharmacological action of the therapeutics and the latest news and press releases. Additionally, the report provides an overview of the key players involved in therapeutic development for Glycogen Storage Disorders (GSD) and features dormant and discontinued products.

GlobalData tracks 23 drugs in development for Glycogen Storage Disorders (GSD) by 18 companies/universities/institutes. The top development phase for Glycogen Storage Disorders (GSD) is preclinical with 12 drugs in that stage. The Glycogen Storage Disorders (GSD) pipeline has 21 drugs in development by companies and two by universities/ institutes. Some of the companies in the Glycogen Storage Disorders (GSD) pipeline products market are: Golden Heart Flower, Beam Therapeutics and Liberyx Therapeutics.

The key targets in the Glycogen Storage Disorders (GSD) pipeline products market include Glucose 6 Phosphatase (G6Pase or Glucose 6 Phosphatase Alpha or G6PC or EC 3.1.3.9), Lysosome Associated Membrane Glycoprotein 2 (CD107 Antigen Like Family Member B or LGP96 or CD107b or LAMP2), and Peroxisome Proliferator Activated Receptor Delta (NUCI or Nuclear Hormone Receptor 1 or Nuclear Receptor Subfamily 1 Group C Member 2 or Peroxisome Proliferator Activated Receptor Beta or NR1C2 or PPARD).

The key mechanisms of action in the Glycogen Storage Disorders (GSD) pipeline product include Glucose 6 Phosphatase (G6Pase or Glucose 6 Phosphatase Alpha or G6PC or EC 3.1.3.9) Activator with six drugs in Phase III. The Glycogen Storage Disorders (GSD) pipeline products include four routes of administration with the top ROA being Oral and five key molecule types in the Glycogen Storage Disorders (GSD) pipeline products market including Small Molecule, and Gene Therapy.

Glycogen Storage Disorders (GSD) overview

Glycogen storage diseases (GSDs) constitute inherited inborn errors in carbohydrate metabolism, with clinical manifestations emerging from neonatal stages to adulthood. Typically, these disorders arise from deficiencies in specific enzymes crucial for glycogen breakdown, leading to abnormal glycogen accumulation in the liver or skeletal muscles. The incapacity to mobilize glucose from glycogen results in hypoglycemia and exercise-induced weakness, contributing to enduring complications. The intricate nature of these metabolic disruptions underscores the importance of understanding GSDs for timely diagnosis and management, addressing both immediate symptoms such as hypoglycemia, and long-term consequences like exercise-induced weakness.

For a complete picture of Glycogen Storage Disorders (GSD)’s pipeline drug market, buy the report here.

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GlobalData’s pipeline drugs offers detailed profiles of pharmaceutical drugs in all stages of pre-clinical and clinical development, from discovery through to pre-registration. Coverage is limited to novel human medicinal drugs and biosimilars seeking market approval proprietary and is one of two primary repositories of pharmaceutical drug information offered by GlobalData through its Pharmaceutical Intelligence Center.