Paroxysmal Nocturnal Hemoglobinuria is an indication for drug development with over 40 pipeline drugs currently active. According to GlobalData, preregistered drugs for Paroxysmal Nocturnal Hemoglobinuria have a 100% likelihood of approval (LoA) indication benchmark. GlobalData’s report assesses how phase transition success rate (PTSR) and likelihood of approval (LoA) scores for pipeline drugs in Paroxysmal Nocturnal Hemoglobinuria compared to historical benchmarks. Buy the report here.

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GlobalData tracks drug-specific phase transition and likelihood of approval scores, in addition to indication benchmarks based off 18 years of historical drug development data. Attributes of the drug, company and its clinical trials play a fundamental role in drug-specific PTSR and likelihood of approval.

Paroxysmal Nocturnal Hemoglobinuria overview

Paroxysmal nocturnal hemoglobinuria is a rare disease in which red blood cells break down earlier than normal. Symptoms include abdominal pain, back pain, dark urine, easy bruising or bleeding, headache, and shortness of breath. The predisposing factors include age, obesity, and hormone therapy. Treatment includes surgery, chemotherapy, and radiation therapy.

For a complete picture of PTSR and LoA scores for drugs in Paroxysmal Nocturnal Hemoglobinuria, buy the report here.

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GlobalData, the leading provider of industry intelligence, provided the underlying data, research, and analysis used to produce this article. 

GlobalData’s Likelihood of Approval analytics tool dynamically assesses and predicts how likely a drug will move to the next stage in clinical development (PTSR), as well as how likely the drug will be approved (LoA). This is based on a combination of machine learning and a proprietary algorithm to process data points from various databases found on GlobalData’s Pharmaceutical Intelligence Center.