RPL-301 is under clinical development by Rocket Pharmaceuticals and currently in Phase I for Anemia. According to GlobalData, Phase I drugs for Anemia have an 82% phase transition success rate (PTSR) indication benchmark for progressing into Phase II. GlobalData’s report assesses how RPL-301’s drug-specific PTSR and Likelihood of Approval (LoA) scores compare to the indication benchmarks. Buy the report here.
GlobalData tracks drug-specific phase transition and likelihood of approval scores, in addition to indication benchmarks based off 18 years of historical drug development data. Attributes of the drug, company and its clinical trials play a fundamental role in drug-specific PTSR and likelihood of approval.
RPL-301 overview
RPL-301 is under development for the treatment of pyruvate kinase deficiency. The therapeutic candidate constitutes patient-derived immature bone marrow cells (called CD34+) genetically modified with a lentivirus to express pyruvate kinase (PKLR) enzyme. It is administered through intravenous route.
Rocket Pharmaceuticals overview
Rocket Pharmaceuticals (Rocket Pharma), formerly Inotek Pharmaceuticals Corp is a clinical-stage biopharmaceutical company. It focuses on
For a complete picture of RPL-301’s drug-specific PTSR and LoA scores, buy the report here.