Huntington’s gene therapy research has reached a turning point, expert says
Despite unanticipated regulatory hurdles following promising clinical results with a novel investigational treatment for Huntington’s Disease, the significance of the…
Industry
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Calls for change as access to cell and gene therapies in the Netherlands falls short
The Netherlands is falling behind other European countries in providing access to advanced therapy medicinal products (ATMPs) according to Peter…
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Autologous versus allogeneic: how cell therapy development is changing in oncology
Cell therapies have gained steam in oncology since Novartis’s Kymriah (tisagenlecleucel) became the first chimeric antigen receptor (CAR)-T cell therapy…
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SLE and LN market expected to reach $5.9bn across 7MM by 2034
A notable growth in the systemic lupus erythematosus (SLE) and lupus nephritis (LN) market across the seven major markets (7MM;…
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JPM26: Solid Biosciences banks on its AAV capsid to catalyse gene therapy success
Solid Biosciences is positioning itself for a potentially “transformative” year as it builds on its 2025 success and centres its…
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Big pharma and investors re-engage in CGTs and race to scale
Panels at the Alliance for Regenerative Medicine’s Industry Briefing highlighted how CGTs are expanding beyond rare disease into broader indications,…
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Investors bet on newer technology and indications for CGTs
As confidence grows for innovative in vivo strategies, some investors are saying they could be the future of the cell…
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Redefining clinical trials in oncology and rare diseases across the Europe
Later this month, experts from the pharmaceutical and biotechnology industry and patient advocacy space will gather in Munich, Germany, to…
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Metagenomi culls 25% of its workforce and replaces CEO in reshuffle
Metagenomi will slash a quarter of its workforce and switch up its CEO as part of efforts to extend its…
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FDA halts uniQure’s plans for Huntington’s disease gene therapy
The path to approval for uniQure’s gene therapy candidate for Huntington’s disease is in doubt as the US Food and…
