rare diseases

PTC Therapeutics to commercialise Akcea’s two rare disease drugs

Ionis Pharmaceuticals affiliate Akcea Therapeutics has signed an agreement with biopharmaceutical company PTC Therapeutics for the commercialisation of its rare…

BioNTech and Genevant Sciences to develop rare disease drugs

German biopharmaceutical firm BioNTech has partnered with Genevant Sciences, a genetic disorder therapeutics maker, to develop mRNA therapy programmes, which…