RCT-1100 is under clinical development by Recode Therapeutics and currently in Phase I for Primary Ciliary Dyskinesia. According to GlobalData, Phase I drugs for Primary Ciliary Dyskinesia does not have sufficient historical data to build an indication benchmark PTSR for Phase I. GlobalData uses proprietary data and analytics to create drugs-specific PTSR and LoA in the RCT-1100 LoA Report. Buy the report here.

GlobalData tracks drug-specific phase transition and likelihood of approval scores, in addition to indication benchmarks based off 18 years of historical drug development data. Attributes of the drug, company and its clinical trials play a fundamental role in drug-specific PTSR and likelihood of approval.

RCT-1100 overview

Oligonucleotide is under development for the treatment of primary ciliary dyskinesia. It is administered through inhalational route. The drug candidate is being developed based Selective Organ Targeting (SORT) lipid nanoparticle (LNP) delivery platform which enables organ specific delivery of RNAs and DNAI1 protein payloads.

Recode Therapeutics overview

Recode Therapeutics is a biopharmaceutical company that carries out discovery and develops therapies for the treatment of respiratory diseases. The company is investigating lead programs by harnessing drug development and regulatory pathways targeting cystic fibrosis and primary ciliary dyskinesia. Recode Therapeutics proprietary SORT LNP delivery platform provides different types of cargo (mRNA, tRNA, CRISPR) multiple delivery systems to advance drug candidates. The company funding partners include Colt Ventures, Ecor1 Capital, Hunt Technology, NS Investment, Pfizer Ventures, Sanofi Ventures and Vida Ventures. It has additional offices in Dallas, Texas, the US. Recode Therapeutics is headquartered in Menlo Park, California, the US.

For a complete picture of RCT-1100’s drug-specific PTSR and LoA scores, buy the report here.

This content was updated on 7 February 2024

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GlobalData, the leading provider of industry intelligence, provided the underlying data, research, and analysis used to produce this article.

GlobalData’s Likelihood of Approval analytics tool dynamically assesses and predicts how likely a drug will move to the next stage in clinical development (PTSR), as well as how likely the drug will be approved (LoA). This is based on a combination of machine learning and a proprietary algorithm to process data points from various databases found on GlobalData’s Pharmaceutical Intelligence Center.