FDA halts uniQure’s plans for Huntington’s disease gene therapy
The company’s stock has plummeted after news of regulatory uncertainty despite positive results.
Cell & Gene Therapy
Sartorius to invest $3m for minority share in biotech start-up Nanotein
Ultragenyx receives complete response letter for UX111 BLA
JCR Pharma and Alexion partner on JUST-AAV gene therapy platform
DoH and Children’s National Hospital link for cell and gene therapy
Caribou cuts pipeline and workforce to focus on lead CAR-T programmes
European agencies catch up with speedier regulatory pathways for CGTs in the US
Inborn errors of metabolism elicit unique challenges for therapy development
